In focus · trending topic

Rare diseases

2 stories · following the connections

PTC Therapeutics Authorizes Up to $500 Million in Share Buybacks

By Helena WardNov 3, 2026, 12:54 PM UTC

UK Grants Conditional Approval to Dojolvi for Rare Fatty Acid Disorders

By Naomi CalderOct 30, 2026, 4:59 PM UTC